Intrathecal Gene Therapy for Giant Axonal Neuropathy
Original Article
D.X. Bharucha-Goebel, J.J. Todd, D. Saade, G. Norato, M. Jain, T. Lehky, R.M. Bailey, J.A. Chichester, R. Calcedo, D. Armao, A.R. Foley, P. Mohassel, E. Tesfaye, B.P. Carlin, B. Seremula, M. Waite, W.M. Zein, L.A. Huryn, T.O. Crawford, C.J. Sumner, A. Hoke, J.D. Heiss, L. Charnas, J.E. Hooper, T.W. Bouldin, E.M. Kang, D. Rybin, S.J. Gray, and C.G. Bönnemann
N Engl J Med 2024;390:1092-1104
Available Credit
- 1.00 AMA PRA Category 1 Credit™
- 1.00 Participation
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